The state-of-the-art information regarding gene therapy has been included in this all-inclusive book. Gene Therapy as a field has gained its due regard after all these years of poor outcomes. Issues in the past which were troubling scientists and practitioners are now being easily resolved. The growth of secure and effective gene transfer and development in the field of cell therapy has now brought new ways to deal with varied diseases. The book aims at compiling information from different resources about various applications and inherited diseases, discussing important topics such as gene therapy for retinitis pigmentosa, primary immunodeficiencies, molecular therapy for lysosomal storage diseases, and clinical and translational challenges in gene therapy of cardiovascular diseases.